The FDA just approved a new treatment for a devastating disease. The price tag is more than $2 million.
- The US FDA just approved a new treatment for a devastating rare genetic disease.
- Called Zolgensma, it is a type of cutting-edge, one-time treatment called a "gene therapy" that treats the disease spinal muscular atrophy at its genetic root.
- That means it should work longer than the typical drug, but has also translated to a much higher price tag, too.
- Zolgensma, which is made by drugmaker Novartis's AveXis unit, will cost $2.125 million, the company said on Friday.
- Visit Business Insider's homepage for more stories.
The FDA just approved a cutting-edge new treatment for a devastating rare genetic disease called spinal muscular atrophy.The treatment, Novartis's Zolgensma, is a one-time therapy that works to treat the disease at the genetic level. That meants the drug's effects should last for a long time, though it's still not known if the treatment will be permanent.Advertisement
Novartis priced the product at $2.125 million, or $425,000 a year if paid over a five-year installment plan. Novartis called the price fair and reasonable on a conference call with reporters on Friday.ICER, a group that measures the cost-effectiveness of new drugs, has said that a fair price range for Zolgensma is likely between $310,000 to $900,000, and could be up to $1.5 million.
- Two more test positive for COVID-19 in Manipur, total cases 34
- Fujifilm launches X-T4 mirrorless digital camera in India
- Syria reports 20 new coronavirus cases
- Elderly woman dies of COVID-19 in HP; with 10 new cases total tally reaches 214
- Airtel’s Africa unit is now a nearly-billion dollar business where every user pays 40% more than the one in India